Investigational gene therapy shows long-term success in AADC
There are currently no approved therapies that address the underlying cause of aromatic L-amino acid decarboxylase (AADC) deficiency.
25th October 2019
Latest news
‘Revolutionary’ liquid sickle cell treatment unveiled
The new formation will enable doctors to personalise doses for young children.
25th October 2019
Xospata bags European Commission approval
The decision was based on the Phase III ADMIRAL trial, in which one-year survival rates shot to 37% for patients who received Xospata, compared to 17% for patients who received salvage chemotherapy.
25th October 2019
First patient enrolled in Oxford BioDynamics’ ALS biomarker study
ALS - amyotrophic lateral sclerosis - is a specific disease that causes the death of neurons controlling voluntary muscles.
25th October 2019
NHS review puts emphasis on vaccine uptake
One in seven five-year-olds may not be fully up to date with some routine immunisations, and the UK has lost its ‘measles-free’ status.
25th October 2019
CR UK, Novartis, Sixth Element team up for hard to treat cancers
The collaboration focuses on the RAS family of genes, which cause more than 30% of all human cancers, including 95% of pancreatic cancers and 45% of colorectal cancers.
24th October 2019
NHSE signs ‘definitive’ agreement for Vertex CF drugs
Even more excitingly, clinicians will be able to begin prescribing the drugs - Orkambi, Symkevi and Kalydeco - within just 30 days.
24th October 2019
GPs call for ‘better training and tech’ for video consultations
Despite promising uptake figures, only 1% of all current consultations are delivered via video link.
24th October 2019
Cosentyx receives EU label update
The drug is the first and only fully-human biologic that directly inhibits interleukin-17A.
24th October 2019
Just one week left to get entered into the 2019 Medical & Scientific Excellence Awards
Entry for the 2019 competition will be closing at midnight on Thursday the 31st October.
24th October 2019
BMS’ Opdivo, Yervoy show promise in lung cancer
The results build on the benefits the combination has previously shown in various indications.
23rd October 2019
Electronic prescriptions could save NHS £300m
The final roll-out phase is set to go live on November 18.
23rd October 2019
Stelara bags positive results in ulcerative colitis
The data were presented at the United European Gastroenterology Week (UEGW) congress.
23rd October 2019
Success for early MLD gene therapy
The treatment is a cryopreserved formulation of OTL-200.
23rd October 2019
Janssen seeks to expand Tremfya in arthritis
Up to a third of the 14 million people who are living with psoriasis in Europe will also develop psoriatic arthritis.
23rd October 2019
